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AI-Powered Orphan Drug Development

Turning off-label use into approved orphan drugs

Our AI platform identifies, validates and accelerates regulatory pathways for rare disease treatments.

73%

Workflow automation with AI

11

Orphan Drug Designations granted

16

FDA Orphan Drug Designation submissions

Rare diseases

300M+

Patients are affected by a rare disease accross the world

95%

of rare diseases have no approved treatment

8 000

Rare Diseases known over the world

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pipeline

Our ambition is to have 30 new drugs in 2030

Newsroom

Latest news

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